How to help
Please get in touch with us directly if you would like to donate to our:
pre-clinical research studies and the NURR1 / NR4A2 cohort study (25+ enrolled) with iPSCs at the University of Miami in Florida, USA (led by Dr Derek Dykxhoorn).
‘natural history’ dataset using aggregate, anonymised data from medical records with Citizen Health.
new biomarker project to develop blood-based biomarkers for NURR1 to support future trials for our community as well as other conditions with NURR1 deficiency or dysregulation.
first clinical Centre of Excellence for treating children, teens and adults with NR4A2-related deficiencies of NURR1.
Contact us
Interested in what we are doing? Fill out some info and we will be in touch shortly. We can’t wait to hear from you!